News & Blog

Text says 'Lafora Disease Therapeutic Overview presented by Dr. Kit Donohue'

Lafora Disease Therapeutic Overview

We invite you to watch a video and read a page about the Lafora Disease Therapeutic Overview as of August 2023.

Are you wondering if there are future therapy options for Lafora Disease? Also, what treatments are in progress?

At last week’s event, Ask the Experts: A Q&A for Lafora Families, Chelsea’s Hope Science Director, Dr. Kit Donohue, shared an overview of treatment options in the pipeline. We are happy to share a short recording from the Q&A, as well as a PDF page with information from the presentation slideshow.

If you registered for the event, we’ve already sent you the full recording and handout. Make sure to check your email!

We hope the Q&A was informative and that participants could get their questions answered. Our team will work on creating handouts on Lafora Disease stages and on the importance of testing siblings of Lafora Disease patients. Please let us know if there are other resources we can provide to help you navigate living with Lafora.

Finally, Chelsea’s Hope is grateful for any volunteer who can translate materials from English to other languages. We encourage you to fill out the volunteer interest form if you can assist us.

Access the Lafora Disease Therapeutic Overview video captions in English HERE.

Access the transcript in Italian HERE.

Please email Dr. Donohue if you have any follow-up questions from the Q&A.

Title text on the left says 'upcoming webinars.' Below is a bullet point list of text that says 'Childhood Dementia Introduction Tue. 5th September 10:30 - 11:30 pm EST Accessing Emerging Treatments for Childhood Dementia Thu. 7th September 6 - 6:45 pm EST We Don't Fit Report Tue. 10th October 9:30 - 10:30 pm EST.' On the right text says 'hosted by: Childhood Dementia Intiative. Colorful ovals are in the top right corner and the Chelsea's Hope Lafora Children Research Fund logo is in the bottom right corner.

Childhood Dementia Webinars

The background is mostly white with gray hexagons. Title text on the left says 'upcoming webinars.' Below is a bullet point list of text that says 'Childhood Dementia Introduction
Tue. 5th September 10:30 - 11:30 pm EST Accessing Emerging Treatments for Childhood Dementia
Thu. 7th September 6 - 6:45 pm EST We Don't Fit Report 
Tue. 10th October 9:30 - 10:30 pm EST.' On the right text says 'hosted by: Childhood Dementia Intiative. Colorful ovals are in the top right corner and the Chelsea's Hope Lafora Children Research Fund logo is in the bottom right corner.

Our friends at Childhood Dementia Initiative are hosting three childhood dementia webinars we want to let you know about!

1. Childhood Dementia Introduction

Tuesday, 5th September 2023 from 10:30 – 11:30 pm EST


2. Accessing Emerging Treatments for Childhood Dementia

Thursday, 7th September from 6 – 6:45 pm EST


3. We Don’t Fit Report

Tuesday, 10th October from 9:30 – 10:30 pm EST


Why attend?

Dementia is one of many symptoms of Lafora Disease. These free webinars could benefit families and caregivers, though healthcare providers, researchers, and advocates who attend could better understand childhood dementia.

Please note: Childhood Dementia Initiative is located in Australia, but the events automatically show up in your timezone when you view the session details. We know the last webinar will conflict with our 2023 Lafora Disease Science Symposium, but wanted to pass along the information if you are signed up to get virtual recordings of the Symposium and available on October 10 to learn about CDI’s report.

Text says 'Ask the experts: a q&a for Lafora families' over a white and gray hexagonal background.

Ask the Experts: A Q&A Session for Lafora Families

Families, do you have questions about therapies and treatment for Lafora Disease? You have a chance to ask the experts!

You’re invited…

📌 EVENT: Ask the Experts: A Q&A Session for Lafora Families
📌 DATE: Monday, August 28, 2023 from 3-4:30 pm EST
📌 LOCATION: Zoom. Please register for the meeting link.

Keep reading for more details about the Q&A!!

The Chelsea's Hope Lafora Children Research Fund logo is on the left. Text says 'ask the experts: a Q&A for Lafora Families' on the right.

Please join us on Monday, August 28th, 3:00 – 4:30 pm EST on Zoom. Our Science Director, Dr. Kit Donohue, will overview the current therapies in development for Lafora Disease. Afterward, several of our researchers and clinicians will be available to answer any questions you have about current treatments and medications.
We want to highlight Dr. Viet-Huong Nguyen, a pharmacist with a special interest in Lafora disease, who will be in attendance. Dr. Nguyen is an associate professor at Chapman University whose research interests include epilepsy. She answered questions from families in attendance at the 2022 Lafora Disease Science Symposium and presented at our June Research Roundtable. We are grateful for her to share her wealth of knowledge again with the community!

So, please come with questions! We would love to have you join us. Please register to receive the Zoom link.

This is a graphic with a headshot of Niki Markou smiling in the center. The background is a purple gradient.

Director of Family Support Announcement

This is a photo of Niki Markou, new Director of Family Support, smiling.Chelsea’s Hope Welcomes First Director of Family Support

We are thrilled to announce our first Director of Family Support is Niki Markou.

She will be responsible for helping to successfully plan, implement, and continually improve Chelsea’s Hope’s support, registry coordination, and patient community support programs. We created this new role to better serve our mission of improving the lives of those affected by Lafora Disease.

Meet the Team

You might know Niki from the Fighting the Rare documentary or her advocacy work. She is a powerful force in the Lafora Disease community! She has served as Marketing and Communications Director on the Board since she joined Chelsea’s Hope in 2020. Her daughter Angelina is the only patient diagnosed with Lafora Disease in Australia, and Niki frequently shares their story to raise awareness with news media, our partner organizations, and via Lafora Initiative.

She is a passionate advocate for her daughter, other Lafora disease patients, and the rare disease community. We hope you will join us in congratulating Niki on her new position! We are grateful for her commitment to improving the lives of those affected by Lafora and advancing the mission of Chelsea’s Hope.