Gene Therapy 101

Questions about gene therapy and Lafora Disease? Access the easy-to-read guide Gene Therapy 101 today.

If you want to read more about gene therapy, this is a good patient-friendly website.

If you have more questions about gene therapy and Lafora Disease, please feel free to contact our Science Director, Dr. Kit Donohue, at katherine@chelseashope.org. 

Access the PDF in Italian, too: L’ABC della terapia genica.