New Research on Gene Therapy and Lafora Body Aggregation in Mice

Dr. Berge Minassian’s lab has developed and tested an AAV gene therapy for Lafora Disease to reduce glycogen synthesis and halt Lafora Body aggregation in mice.

We are still a long way from being able to use gene therapy to treat Lafora Disease, however, this is an important step toward curing it for future generations.

If you have questions about gene therapy and Lafora Disease, check out our easy-to-read guide linked below. Please feel free to contact our Science Director, Dr. Kit Donohue, at

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