EnAble Therapeutics Expanded Access Announcement

EnAble Therapeutics has informed Chelsea’s Hope that it is willing to partner with clinicians to lead a n=1 Expanded Access trial or through the Right to Try Act with their potential therapy for Lafora Disease, VAL-1221.

EnAble has indicated that the following medical resources and support will be needed:
Clinicians with institutional support including internal and external regulatory assistance and treatment / I.V. infusion capability.

EnAble has confirmed that this could be your child’s primary neurologist but EnAble has also confirmed that the clinician does not need to be a neurologist.

If interested, please have your clinician contact:

Vicki Wong
Enable Therapeutics

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