Research Simplified for families

The Latest Research in Lafora Disease – Summarized for Easy Reading

Research Simplified for Families

Interested in learning about the new research developments in Lafora disease in a concise and easy-to-read form?

Keep reading for summaries of some of the latest published research in Lafora disease. Our goal is to make the research easier to read and understand for families. You’ll find the research simplified in one-page PDFs, but we will also link to the full peer-reviewed publications.

1. Early Treatment With Metformin Improves Neurological Outcomes in Lafora Disease

2. Effect of Alglucosidase alfa (Myozyme) Therapy in Lafora Disease

3. Antisense oligonucleotide (ASO) therapy targeting Gys1 gene

4. Identifying CSF and PET scan biomarkers to evaluate progression of Lafora Disease

Questions? Contact Maysoon Hussain (